Skip to main content
OpenTrials

Clinical trial condition

Muscular Dystrophies

Explore clinical trials studying Muscular Dystrophies. Study availability and eligibility vary by location and protocol.

165 public trials 36 recruiting studies
Refine in advanced search Browse all conditions

Muscular Dystrophies trial results

Completed

Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD)

NCT03981289

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb Girdle Muscular Dystrophy, +8 more
Locations
  • University of California Irvine Irvine, California, United States
  • The University of Colorado Anschutz Medical Campus Aurora, Colorado, United States
  • University of Iowa Iowa City, Iowa, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
View Trial Details
Completed

Safety, Tolerability, PK, and PD Study of PGN-EDODM1 in Participants With Myotonic Dystrophy Type 1

NCT06204809

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
Locations
  • UCI Center for Clinical Research Irvine, California, United States
  • Stanford University Palo Alto, California, United States
  • Rare Disease Research Atlanta, Georgia, United States
  • University of Kansas Medical Center Fairway, Kansas, United States
View Trial Details
Completed

A Study to Assess Vamorolone in Boys Ages 2 to <4 Years and 7 to <18 Years With Duchenne Muscular Dystrophy (DMD)

NCT05185622

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Alberta's Children Hospital Calgary, Alberta, Canada
  • British Columbia Children's Hospital Vancouver, British Columbia, Canada
  • Children's Hospital of Eastern Ontario Ottawa, Ontario, Canada
  • The Hospital for Sick Children Toronto, Ontario, Canada
View Trial Details
Completed

A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD)

NCT05096221

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Little Rock, Arkansas, United States
  • UC San Diego Altman Clinical and Translational Research Institute La Jolla, California, United States
  • UCLA Medical Center Los Angeles, California, United States
  • Lucile Packard Children's Hospital at Stanford Palo Alto, California, United States
View all 42 locations
View Trial Details
Completed

A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy

NCT03406780

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
Locations
  • University of California, Davis Sacramento, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Nemours Children's Hospital Orlando, Florida, United States
  • University of Iowa Iowa City, Iowa, United States
View Trial Details
Completed

Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases

NCT02532244

Conditions
Amyotrophic Lateral Sclerosis, Central Nervous System Diseases, Charcot-Marie-Tooth Disease, +28 more
Locations
  • Nemours Children's Hospital Delaware Wilmington, Delaware, United States
  • Nemours Children's Specialty Care Jacksonville, Florida, United States
  • Nemours Children's Hospital Orlando Orlando, Florida, United States
View Trial Details
Completed

LAMA2 Genetic Correction

NCT06582537

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, MDC1A, +6 more
Locations
  • Academisch Ziekenhuis Maastricht Maastricht, Limburg, Netherlands
View Trial Details

Related conditions