NCT05200702
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital Myopathy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +19 more
- Locations
-
- Institute of Myology Paris, France
Clinical trial condition
Muscular Dystrophies
Explore clinical trials studying Muscular Dystrophies. Study availability and eligibility vary by location and protocol.
163 public trials
35 recruiting studies
Muscular Dystrophies trial results
NCT04694456
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Muscular Diseases, +5 more
- Locations
-
- CHU de NICE Nice, France
NCT03179631
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +8 more
- Locations
-
- Phoenix Childrens Hospital Phoenix, Arizona, United States
- Children's Hospital of Los Angeles Los Angeles, California, United States
- University of California, San Francisco (UCSF) - Benioff Children's Hospital - Oakland Oakland, California, United States
- Stanford University Medical Center Palo Alto, California, United States
NCT03981289
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb Girdle Muscular Dystrophy, +8 more
- Locations
-
- University of California Irvine Irvine, California, United States
- The University of Colorado Anschutz Medical Campus Aurora, Colorado, United States
- University of Iowa Iowa City, Iowa, United States
- University of Kansas Medical Center Kansas City, Kansas, United States
Completed
Safety, Tolerability, PK, and PD Study of PGN-EDODM1 in Participants With Myotonic Dystrophy Type 1
NCT06204809
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
- Locations
-
- UCI Center for Clinical Research Irvine, California, United States
- Stanford University Palo Alto, California, United States
- Rare Disease Research Atlanta, Georgia, United States
- University of Kansas Medical Center Fairway, Kansas, United States
NCT05185622
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Alberta's Children Hospital Calgary, Alberta, Canada
- British Columbia Children's Hospital Vancouver, British Columbia, Canada
- Children's Hospital of Eastern Ontario Ottawa, Ontario, Canada
- The Hospital for Sick Children Toronto, Ontario, Canada
Completed
Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients
NCT05479981
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +11 more
- Locations
-
- University of California Los Angeles Los Angeles, California, United States
- Stanford University Palo Alto, California, United States
- University of Colorado Denver, Colorado, United States
- University of Florida Gainesville, Florida, United States
NCT05166109
- Conditions
- Becker Muscular Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +8 more
- Locations
-
- University of Pittsburgh Pittsburgh, Pennsylvania, United States
- Azienda Ospedale Universita Padova Padova, Italy
NCT05096221
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- Arkansas Children's Little Rock, Arkansas, United States
- UC San Diego Altman Clinical and Translational Research Institute La Jolla, California, United States
- UCLA Medical Center Los Angeles, California, United States
- Lucile Packard Children's Hospital at Stanford Palo Alto, California, United States
Completed
A Study of CAP-1002 in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy
NCT03406780
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
- Locations
-
- University of California, Davis Sacramento, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Nemours Children's Hospital Orlando, Florida, United States
- University of Iowa Iowa City, Iowa, United States