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Clinical trial condition

Muscular Dystrophies

Explore clinical trials studying Muscular Dystrophies. Study availability and eligibility vary by location and protocol.

165 public trials 36 recruiting studies
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Muscular Dystrophies trial results

Active, not recruiting

A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy

NCT05126758

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • UCSD Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Children's Hospital of Los Angeles, Division of Neurology Los Angeles, California, United States
View all 20 locations
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Active, not recruiting

A Study to Evaluate the Safety of AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)

NCT05230459

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, FKRP, FKRP Mutation, +17 more
Locations
  • University of California - Irvine Irvine, California, United States
  • University of Iowa Iowa City, Iowa, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
  • Kennedy Krieger Institute Baltimore, Maryland, United States
View Trial Details
Active, not recruiting

A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)

NCT06185764

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +15 more
Locations
  • Stanford Neuromuscular Research San Carlos, California, United States
  • University of Florida Clinical Research Center Gainesville, Florida, United States
  • University of Kansas Medical Center Fairway, Kansas, United States
  • Boston Children's Hospital Boston, Massachusetts, United States
View all 26 locations
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Active, not recruiting

A First-in-human Study of EPI-321 in Facioscapulohumeral Muscular Dystrophy

NCT06907875

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Facioscapulohumeral Muscular Dystrophy, Genetic Diseases, Inborn, +7 more
Locations
  • David Geffen School of Medicine at University of California, Los Angeles Los Angeles, California, United States
  • Rare Disease Research Atlanta, Georgia, United States
  • Kennedy Krieger Institute, Center for Genetic Muscle Disorders Baltimore, Maryland, United States
  • University of Massachusetts Chan Medical School Worcester, Massachusetts, United States
View Trial Details
Active, not recruiting

Phase 2 Open-label Extension Study of AOC 1020 in Participants With Facioscapulohumeral Muscular Dystrophy (FSHD)

NCT06547216

Conditions
Atrophies, Facioscapulohumeral, Atrophy, Facioscapulohumeral, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +33 more
Locations
  • University of California Los Angeles Los Angeles, California, United States
  • Stanford University Palo Alto, California, United States
  • University of California San Diego San Diego, California, United States
  • University of Colorado Denver, Colorado, United States
View all 17 locations
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Active, not recruiting

A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice

NCT04475926

Conditions
Cardiomyopathies, Cardiovascular Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
Locations
  • Barrow Neurological Institute Phoenix, Arizona, United States
  • Arkansas Children's Little Rock, Arkansas, United States
  • University of California San Diego La Jolla, California, United States
  • University of California, Davis Health Dept of PM&R Sacramento, California, United States
View all 26 locations
View Trial Details

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