Completed
Phase 3 Study of Ataluren in Participants With Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
NCT01826487
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
- Locations
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- University of California, Los Angeles Los Angeles, California, United States
- UC Davis Medical Center Sacramento, California, United States
- Children's Hospital Colorado - Center for Cancer and Blood Disorders Aurora, Colorado, United States
- Child Neurology Center of Northwest Florida Gulf Breeze, Florida, United States