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Clinical trial condition

Neuromuscular Diseases

Explore clinical trials studying Neuromuscular Diseases. Study availability and eligibility vary by location and protocol.

266 public trials 62 recruiting studies
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Neuromuscular Diseases trial results

Recruiting

A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping

NCT07587242

Conditions
Congenital, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, +22 more
Locations
  • AP-HP Hospital Armand-Trousseau Paris, France
  • Universitaetsklinikum Essen Essen, Germany
  • Universitaetsklinikum Heidelberg Heidelberg, Germany
  • Klinikum der Ludwig-Maximilians-Universitaet Muenchen München, Germany
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Recruiting

Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

NCT07287189

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne, +10 more
Locations
  • University of California Los Angeles Los Angeles, California, United States
  • Colorado Children's Aurora, Colorado, United States
  • Lurie Children's Chicago, Illinois, United States
  • UMass Memorial Medical Center Worcester, Massachusetts, United States
View all 21 locations
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Recruiting

VirtualPark_Pediatric

NCT07580365

Conditions
Congenital Myopathies, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dystrophinopathy, +11 more
Locations
  • IRCCS E. Medea - La Nostra Famiglia Bosisio Parini, LC, Italy
  • IRCCS Fondazione Stella Maris Pisa, PI, Italy
  • IRCCS Fondazione Mondino Pavia, PV, Italy
  • Fondazione Don Gnocchi - Centro "S. Maria al Mare" Salerno, SA, Italy
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Recruiting

A Study to Investigate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AZD5492 in Adult Participants With Systemic Lupus Erythematosus or Idiopathic Inflammatory Myopathies or Rheumatoid Arthritis.

NCT06916806

Conditions
Arthritis, Arthritis, Rheumatoid, Autoimmune Diseases, +17 more
Locations
  • Research Site Anniston, Alabama, United States
  • Research Site Birmingham, Alabama, United States
  • Research Site La Jolla, California, United States
  • Research Site Sacramento, California, United States
View all 37 locations
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Recruiting

A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)

NCT07282847

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
Locations
  • Barrow Neurological Institute Phoenix, Arizona, United States
  • University of California, Irvine (UCI) Irvine, California, United States
  • Stanford Neuroscience Health Center Palo Alto, California, United States
  • NYU Langone New York, United States
View Trial Details

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