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Clinical trial condition

Mucopolysaccharidoses

Explore clinical trials studying Mucopolysaccharidoses. Study availability and eligibility vary by location and protocol.

193 public trials 26 recruiting studies
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Mucopolysaccharidoses trial results

Completed

A Study to Assess the Safety, Tolerability, and Efficacy of Long-term SOBI003 Treatment in Pediatric MPS IIIA Patients

NCT03811028

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Children´s Hospital and research center Oakland, California, United States
  • University of North Carolina hospitals Chapel Hill, North Carolina, United States
  • Gazi University Hospital Ankara, Turkey (Türkiye)
View Trial Details
Completed

A Study to Assess the Safety and Tolerability of SOBI003 in Pediatric MPS IIIA Patients

NCT03423186

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Childrens's Hospital and Research Center Oakland, California, United States
  • University of North Carolina Hospitals Chapel Hill, North Carolina, United States
  • University Medical Center Hamburg-Eppendorf Hamburg, Germany
  • Gazi University Hospital Ankara, Turkey (Türkiye)
View Trial Details
Completed

Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome)

NCT01415427

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
Locations
  • Phoenix, Arizona, United States
  • Oakland, California, United States
  • Orange, California, United States
  • Wilmington, Delaware, United States
View all 43 locations
View Trial Details
Completed

Screening Study to Identify Pediatric Patients With Hunter Syndrome Who Demonstrate Evidence of Central Nervous System (CNS) Involvement and Who Are Currently Receiving Treatment With Elaprase®

NCT00937794

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
  • Birmingham Children's Hospital Birmingham, United Kingdom
View Trial Details

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