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Clinical trial condition

Mucopolysaccharidoses

Explore clinical trials studying Mucopolysaccharidoses. Study availability and eligibility vary by location and protocol.

192 public trials 30 recruiting studies
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Mucopolysaccharidoses trial results

Completed

Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II Patients Receiving Idursulfase

NCT00630747

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +24 more
Locations
  • St. Joseph's Hospital Phoenix, Arizona, United States
  • Pediatric Clinical Research Center, Children's Hospital Oakland Oakland, California, United States
  • The Children's Hospital Denver, Colorado, United States
  • Harbin Clinic Rome, Georgia, United States
View all 52 locations
View Trial Details
Completed

Iduronate-2-sulfatase Enzyme Replacement Therapy in Mucopolysaccharidosis II (MPS II)

NCT00069641

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +22 more
Locations
  • Children's Hospital Oakland Oakland, California, United States
  • St. Louis Children's Hospital, Washington University St Louis, Missouri, United States
  • University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
  • Texas Children's Hospital, Baylor College of Medicine Houston, Texas, United States
View Trial Details
Completed

Collection and Study of Cerebrospinal Fluid in Patients With Hunter Syndrome

NCT01449240

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations
  • Emory University Decatur, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
  • Children's Hospitals and Clinics of Minnesota Minneapolis, Minnesota, United States
  • University of North Carolina, Division of Genetics and Metabolism Chapel Hill, North Carolina, United States
View Trial Details
Completed

Safety and Clinical Outcomes in Hunter Syndrome Patients 5 Years of Age and Younger Receiving Idursulfase Therapy

NCT00607386

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +24 more
Locations
  • Hospital de Clinicas de Porto Alegre, Servico de Genetica Medica Porto Alegre, Rio Grande do Sul, Brazil
  • Instytut Pomnik Centrum Zdrowia Dziecka, Klinika Chorob Metaboliczynch, Endokrynologii i Diabetologii Warsaw, Poland
  • National Taiwan University Hospital, Dept. of Pediatrics and Medical Genetics Taipei, Taiwan
View Trial Details
Completed

Randomized, Controlled, Open-label, Multicenter, Safety and Efficacy Study of rhHNS Administration Via an IDDD in Pediatric Patients With Early Stage MPS IIIA Disease

NCT02060526

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +18 more
Locations
  • Los Angeles Biomedical Research Torrance, California, United States
  • University of Minnesota Department of Pediatrics Minneapolis, Minnesota, United States
  • University of North Carolina Chapel Hill, North Carolina, United States
  • Hospital Universitario Austral A Unidad de Investigacion Buenos Aires, Argentina
View Trial Details
Completed

An Observational Study Evaluating Anti-Idursulfase Serum Antibody Response in Hunter Syndrome Patients

NCT00882921

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
Locations
  • Children's Hospital & Research Center Oakland Oakland, California, United States
  • Children's Hospitals and Clinics of Minnesota, Division of Genetics Minneapolis, Minnesota, United States
  • Hospital de Clinicas de Porto Alegre, Servico de Genetica Medica Porto Alegre, Rio Grande do Sul, Brazil
  • Birmingham Children's Hospital Birmingham, United Kingdom
View Trial Details
Completed

S 81694 Plus Paclitaxel in Metastatic Breast Cancer

NCT03411161

Conditions
Breast Diseases, Breast Neoplasms, Carbohydrate Metabolism, Inborn Errors, +17 more
Locations
  • Institut Jules Bordet Clinique Oncologie Médicale Brussels, Belgium
  • UZ Leuven Campus Gasthuisberg Dept. of General Medical Leuven, Belgium
  • Institut de Cancérologie de l'Ouest site Saint Herblain Saint-Herblain, France
  • Chiba cancer center Breast surgery Chiba, Japan
View Trial Details
Completed

Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)

NCT00214773

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • University of California, Irvine Irvine, California, United States
  • Children's Hospital of Los Angeles Los Angeles, California, United States
  • Children's Hospital and Research Center Oakland Oakland, California, United States
  • Emory University Decatur, Georgia, United States
View all 50 locations
View Trial Details
Completed

Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B)

NCT01509768

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Children's Hospital and Research Center Oakland, California, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • Johannes Gutenberg University Medical Center Mainz, Germany
  • Great Ormond Street Hospital for Children London, United Kingdom
View Trial Details

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