Active, Not Recruiting
Phase I/II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA
NCT06095388
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
-
- Universitätsklinikum Hamburg-Eppendorf Hamburg, Germany