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Mucinoses

Clinical trial condition

Mucinoses

Explore clinical trials studying Mucinoses. Study availability and eligibility vary by location and protocol.

239 public trials 34 recruiting studies

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Mucinoses trial results

Active, Not Recruiting

A Phase III Study of JR-141 in Patients With Mucopolysaccharidosis II (STARLIGHT)

NCT04573023

Conditions: Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
Locations: Phoenix Children's Hospital Phoenix, Arizona, United States

UCSF Benioff Children's Hospital Oakland Oakland, California, United States

Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States

University of Minnesota Minneapolis, Minnesota, United States

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Active, Not Recruiting

Impact of B. Adolescentis iVS-1 Probiotic on Gastrointestinal Outcomes

NCT07408518

Conditions: Abdominal Pain, Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +21 more
Locations: People Science, Inc. Los Angeles, California, United States

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Active, Not Recruiting

Gene Therapy With Modified Autologous Hematopoietic Stem Cells for Patients With Mucopolysaccharidosis Type II

NCT05665166

Conditions: Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
Locations: Manchester University Foundation Trust Manchester, United Kingdom

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Active, Not Recruiting

Safety and Efficacy of Voxzogo for Growth Deficits in MPS IVA and VI

NCT05845749

Conditions: Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
Locations: UCSF Benioff Children's Hospital Oakland Oakland, California, United States

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Active, Not Recruiting

Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I, II, and VI

NCT03153319

Conditions: Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +18 more
Locations: The Lundquist Institute at Harbor-UCLA Medical Center Torrance, California, United States

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Active, Not Recruiting

Cardiovascular Structure and Function in the Mucopolysaccharidoses

NCT05063435

Conditions: Carbohydrate Metabolism, Inborn Errors, Cardiac Disease, Cardiovascular Diseases, +15 more
Locations: Children's Hospital of Orange County Orange, California, United States

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Active, Not Recruiting

MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis

NCT02171104

Conditions: Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more
Locations: Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States

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Active, Not Recruiting

A Study to Investigate the Efficacy and Safety of OTL-203 in Subjects With MPS-IH Compared With Standard of Care With Allogeneic HSCT

NCT06149403

Conditions: Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations: University of Minnesota, Pediatrics Minneapolis, Minnesota, United States

Ospedale San Raffaele Milan, Italy

Princess Maxima Center Utrecht, Netherlands

UMC Utrecht Utrecht, Netherlands

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Active, Not Recruiting

Extension Study of Idursulfase-IT Along With Elaprase in Children and Adults With Hunter Syndrome and Cognitive Impairment

NCT06031259

Conditions: Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
Locations: M.A.G.I.C. Clinic Calgary, Alberta, Canada

University of British Columbia Vancouver, British Columbia, Canada

Hospital for Sick Children Toronto, Ontario, Canada

Hopital Femme Mere Enfant Bron, Auvergne-Rhône-Alpes, France

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Active, Not Recruiting

Evaluation of Intravenous Laronidase Pharmacokinetics Before and After Hematopoietic Cell Transplantation in Patients With Mucopolysaccharidosis Type IH.

NCT05634512

Conditions: Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +11 more
Locations: University of Minnesota Masonic Cancer Center Minneapolis, Minnesota, United States

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Mucinoses

Mucinoses trial results

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