NCT00351156
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
- Locations
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- University of California - San Francisco San Francisco, California, United States
- University Research Foundation for Lysosomal Storage Diseases, Inc. Coral Springs, Florida, United States
- Emory University Lysosomal Storage Disease Center Decatur, Georgia, United States
- National Institute of Neurological Disorders and Stroke, NIH Bethesda, Maryland, United States