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Clinical trial condition

Metabolism, Inborn Errors

Explore clinical trials studying Metabolism, Inborn Errors. Study availability and eligibility vary by location and protocol.

114 public trials 18 recruiting studies
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Metabolism, Inborn Errors trial results

Completed

An Open-label Extension Study to Assess the Long-term Safety and Efficacy of ISIS 301012 (Mipomersen) in Patients With Familial Hypercholesterolemia or Severe-Hypercholesterolemia

NCT00694109

Conditions
Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, +14 more
Locations
  • Mission Viejo, California, United States
  • Newport Beach, California, United States
  • Bridgeport, Connecticut, United States
  • Melbourne, Florida, United States
View all 33 locations
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Completed

Study of NTBC for Tyrosinemia I

NCT00004443

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Genetic Diseases, Inborn, +7 more
Locations
  • Oregon Health Sciences University Portland, Oregon, United States
  • University of Washington School of Medicine Seattle, Washington, United States
  • Hopital Sainte Justine Montreal, Quebec, Canada
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