NCT07277361
- Conditions
- Aged 65 Years or Older, Alpha Galactosidase A Deficiency, Brain Diseases, +22 more
- Locations
-
- Groupe Hospitalier Diaconesses Croix Saint-Simon Paris, France
Clinical trial condition
Lysosomal Storage Diseases
Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.
717 public trials
126 recruiting studies
Lysosomal Storage Diseases trial results
NCT07235709
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Division of Cardiology, Yonsei Cardiovascular Hospital, Yonsei University College of Medicine Seoul, South Korea
NCT05247645
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
-
- Irccs Istituto Ortopedico Rizzoli Bologna, Emilia-Romagna, Italy
Recruiting
A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients
NCT06663358
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- University of Alabama at Birmingham Birmingham, Alabama, United States
- Emory University School of Medicine Atlanta, Georgia, United States
- Northwestern University - Feinberg School of Medicine - Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- University of Iowa Hospitals and Clinics Iowa City, Iowa, United States
NCT04885179
- Conditions
- Addison Disease, Adrenal Gland Diseases, Adrenal Insufficiency, +28 more
- Locations
-
- University of California San Francisco San Francisco, California, United States
Recruiting
The Myelin Disorders Biorepository Project
NCT03047369
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
-
- Children's Hospital of Los Angeles Los Angeles, California, United States
- Children's Hospital of Orange County Orange, California, United States
- Stanford University (Lucile Packard Children's Hospital) Palo Alto, California, United States
- University of California, Davis (UC Davis Health) Sacramento, California, United States
NCT04925349
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +37 more
- Locations
-
- AP-HP Hôpital Bicêtre Le Kremlin-Bicêtre, France
- AP-HP Hôpital La Pitié Salpêtrière Paris, France
NCT06488924
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
-
- Hiroshima University Hospital Hiroshima, Japan
- University of the Ryukyus Hospital Okinawa, Japan
- National Center for Child Health and Development Tokyo, Japan
NCT06614894
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +11 more
- Locations
-
- Lysosomal & Rare Disorders Research & Treatment Center, Inc. Fairfax, Virginia, United States
NCT04252066
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Amicus Therapeutics, Inc. Pregnancy Registry Philadelphia, Pennsylvania, United States