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Clinical trial condition

Lysosomal Storage Diseases

Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.

717 public trials 126 recruiting studies
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Lysosomal Storage Diseases trial results

Recruiting

Study to Evaluate the Safety, PK, PD, and Efficacy of PRX-102 in Japanese Patients With Fabry Disease

NCT05710692

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Fukuoka University Chikushi Hospital Chikushino-shi, Fukuoka, Japan
  • Tohoku University Hospital Sendai, Miyagi, Japan
  • University of the Ryukyu Hospital Nishihara, Okinawa, Japan
  • Osaka University Hospital Suita, Osaka, Japan
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Recruiting

A Global Prospective Observational Registry of Patients With Pompe Disease

NCT06121011

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
Locations
  • University of Arkansas Medical Science Little Rock, Arkansas, United States
  • University of California Irvine Irvine, California, United States
  • Wolfson Children's Hospital Jacksonville, Florida, United States
  • Emory University Atlanta, Georgia, United States
View all 41 locations
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Recruiting

MPS (RaDiCo Cohort) (RaDiCo-MPS)

NCT06036693

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +33 more
Locations
  • Centre Hospitalier Universitaire d'Angers Angers, France
  • Hôpital des Enfants - Groupe Hospitalier Pellegrin Bordeaux, France
  • Hôpital Morvan Brest, France
  • Hôpital d'Estaing Clermont-Ferrand, France
View all 23 locations
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Recruiting

GammaGA: Prevalence of Acid Sphingomyelinase Deficiency Disease (ASMD) and Gaucher Disease in Patients With Monoclonal Gammopathies and/or Multiple Myeloma

NCT05992532

Conditions
Acid Sphingomyelinase Deficiency, Blood Protein Disorders, Brain Diseases, +38 more
Locations
  • Hospital Universitario de Álava Vitoria-Gasteiz, Alava, Spain
  • Hospital Universitario Torrecárdenas Almería, Spain
  • Hospital Son Espases Palma de Mallorca, Balearic Islands, Spain
  • Hospital Parc Taulí Sabadell, Barcelona, Spain
View all 23 locations
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