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Clinical trial condition

Lysosomal Storage Diseases

Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.

710 public trials 130 recruiting studies

Lysosomal Storage Diseases trial results

Conditions
Alpha-Mannosidosis, Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +7 more
Locations
  • Kinderneurologie Metabole Ziekten, UZ Brussel, Laarbeeklaan 101 Brussels, Belgium
  • Center for Metabolic Diseases, Department of Clinical Genetics, Juliane Marie Centre, Copenhagen University Hospital, Blegdamsvej 9 Copenhagen, Denmark
  • Servicio de Pediatría, Hospital Materno Infantil, Reina Sofía, Avda Menéndez Pidal sn Córdoba, Spain
  • Genetic Medicine, 6th floor, St Mary's Hospital, Oxford Road, Manchester, United Kingdom
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
Locations
  • UCSF MS Center San Francisco, California, United States
  • Yale University School of Medicine New Haven, Connecticut, United States
  • Emory University Medical Genetics Decatur, Georgia, United States
  • University of Kansas Medical Center, Division of Hematology/Oncology, Dept. of Medicine Westwood, Kansas, United States
View all 18 locations
Conditions
Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +19 more
Locations
  • Children's Hospital and Research Center - Oakland Oakland, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Children's Hospital Boston Boston, Massachusetts, United States
  • Queens Hospital Center Jamaica, New York, United States
View all 18 locations
Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • New York University New York, United States
  • New York, United States
  • Aprillus Asistencia e Investigación Buenos Aires, Argentina
  • Hospital de Oncologia Maria Curie Buenos Aires, Argentina
View all 17 locations