NCT02152189
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +21 more
- Locations
-
- Zentrum für Kinder- und Jugendmedizin Heidelberg, Germany
Clinical trial condition
Lysosomal Storage Diseases
Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.
710 public trials
130 recruiting studies
Lysosomal Storage Diseases trial results
Completed
Observational Study for Subjects With Pompe Disease Undergoing Immune Modulation Therapies
NCT01451879
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +13 more
- Locations
-
- University of Florida Gainesville, Florida, United States
NCT02372513
- Conditions
- Cholesterol Ester Storage Disease, Cholesteryl Ester Storage Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
- Locations
-
- Ankara University School of Medicine Ankara, Turkey (Türkiye)
NCT00074516
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystinosis, Genetic Diseases, Inborn, +4 more
- Locations
-
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
Completed
A Study to Test the Possibility of Cross Reaction Induced by the Idursulfase Drug to GSK2788723
NCT01602601
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
- Locations
-
- GSK Investigational Site Tokyo, Japan
NCT02437253
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +24 more
- Locations
-
- Los Angeles Biomedical Research Institute at Harbor-UCLA Medical Center Torrance, California, United States
NCT01999257
- Conditions
- Autonomic Nervous System Diseases, Brain Diseases, Brain Diseases, Metabolic, +33 more
- Locations
-
- Montreal General Hospital (MUHC) Montreal, Quebec, Canada
NCT01730469
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- GSK Investigational Site Costa Mesa, California, United States
- GSK Investigational Site Miami, Florida, United States
- GSK Investigational Site Miami, Florida, United States
- GSK Investigational Site Orlando, Florida, United States
NCT02770625
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
Not specified
NCT00244582
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- National Institute of Neurological Disorders and Stroke (NINDS) Bethesda, Maryland, United States