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Clinical trial condition

Lysosomal Storage Diseases

Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.

710 public trials 130 recruiting studies
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Lysosomal Storage Diseases trial results

Completed

A Phase III Trial to Assess the Safety and Efficacy of Plant Cell Expressed GCD in Patients With Gaucher Disease

NCT00376168

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations
  • University Research Foundation for Lysosomal Storage Diseases Coral Springs, Florida, United States
  • Division of Medical Genetics, Emory University School of Medicine Decatur, Georgia, United States
  • New York University Medical Center New York, United States
  • Mount Sinai Hospital Toronto, Ontario, Canada
View Trial Details
Completed

Plant Cell Expressed Recombinant Human Glucocerebrosidase Extension Trial

NCT00705939

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations
  • Department of Human Genetics, Emory University School of Medicine Decatur, Georgia, United States
  • Neurogenetics, NYU at Rivergate New York, United States
  • Bone Marrow Transplant Service, The Royal Melbourne Hospital Parkville, Victoria, Australia
  • Mount Sinai Hospital Toronto, Ontario, Canada
View Trial Details
Completed

Safety and Dose Ranging Study of Insulin Receptor MoAb-IDS Fusion Protein in Patients With Hunter Syndrome

NCT02262338

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +22 more
Locations
  • Children's Hospital Oakland Oakland, California, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Emory University Decatur, Georgia, United States
  • ZKJM MC University of Mainz Mainz, Germany
View Trial Details

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