Skip to main content
OpenTrials

Clinical trial condition

Lysosomal Storage Diseases

Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.

710 public trials 130 recruiting studies
Refine in advanced search Browse all conditions

Lysosomal Storage Diseases trial results

Completed

The Efficacy and Safety of Switch Between Agalsidase Beta to Agalsidase Alfa for Enzyme Replacement in Patients With Anderson-Fabry Disease

NCT01268241

Conditions
Anderson-Fabry Disease, Brain Diseases, Brain Diseases, Metabolic, +21 more
Locations
  • Juan Fernandez Hospital, Department of Neurology Buenos Aires, Argentina
  • Unidad Renal Corrientes SRL, Medicina Interna Nefrólogo Corrientes, Argentina
  • UZA - University Ziekenhuis Antwerpen) Edegem, Belgium
  • University Hospital "Sestre Milosrdnice" Department of neuroimmunology and neurogenetic Zagreb, Croatia
View Trial Details
Completed

Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)

NCT00214773

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • University of California, Irvine Irvine, California, United States
  • Children's Hospital of Los Angeles Los Angeles, California, United States
  • Children's Hospital and Research Center Oakland Oakland, California, United States
  • Emory University Decatur, Georgia, United States
View all 50 locations
View Trial Details
Completed

Evaluation of the Long-term Safety, Pharmacodynamics, and Exploratory Efficacy of GZ/SAR402671 in Treatment-Naïve Adult Male Patients With Fabry Disease

NCT02489344

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Investigational Site Number 840002 Atlanta, Georgia, United States
  • Investigational Site Number 840003 Cincinnati, Ohio, United States
  • Investigational Site Number 840001 Fairfax, Virginia, United States
  • Investigational Site Number 250001 Garches, France
View Trial Details
Completed

Home Therapy With VPRIV in Gaucher's Disease

NCT01356537

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations
  • Landeskrankenhaus Bregenz Bregenz, Austria
  • Paracelsus Medizinische Privatuniversität Salzburg Salzburg, Austria
  • AKH, Allgemeines Krankenhaus der Stadt Wien Vienna, Austria
  • Medical University of Vienna Vienna, Austria
View Trial Details
Completed

Home Therapy With Replagal in Fabry Disease

NCT01355146

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Landeskrankenhaus Bregenz Bregenz, Austria
  • LKH-Universitätsklinikum Graz Graz, Austria
  • Paracelsus Medizinische Privatuniversität Salzburg Salzburg, Austria
  • Universitätsklinik für Innere Medizin III Vienna, Austria
View all 22 locations
View Trial Details
Completed

Natural History Study of Patients With Mucopolysaccharidosis Type IIIB (MPS IIIB, Sanfilippo Syndrome Type B)

NCT01509768

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
Locations
  • Children's Hospital and Research Center Oakland, California, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • Johannes Gutenberg University Medical Center Mainz, Germany
  • Great Ormond Street Hospital for Children London, United Kingdom
View Trial Details

Related conditions