NCT01747135
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +23 more
- Locations
-
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
Clinical trial condition
Lysosomal Storage Diseases
Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.
710 public trials
130 recruiting studies
Lysosomal Storage Diseases trial results
NCT01304277
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- University of Alberta Hospital Edmonton, Alberta, Canada
- Queen Elizabeth II Health Sciences Centre Halifax, Nova Scotia, Canada
- The Hospital for Sick Children Toronto, Ontario, Canada
- INC Research Toronto, Ontario, Canada
NCT01710813
- Conditions
- Anaphylaxis, Brain Diseases, Brain Diseases, Metabolic, +17 more
- Locations
-
- Investigational Site Number 840016 Phoenix, Arizona, United States
- Investigational Site Number 840002 Durham, North Carolina, United States
- Investigational Site Number 840004 Hershey, Pennsylvania, United States
- Investigational Site Number 840014 Pittsburgh, Pennsylvania, United States
NCT02765828
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more
- Locations
-
- Duke University Medical Center Durham, North Carolina, United States
NCT00430625
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +15 more
- Locations
-
- Hipolito Yrigoyen Buenos Aires, Argentina
- Shaare Zedek Medical Center Jerusalem, Israel
- Sociedad Espanola de Socorros Mutuos Asunción, Paraguay
- National Research Center for Haematology Moscow, Russia
Completed
Study of Velaglucerase Alfa Enzyme Replacement Therapy in Japanese Patients With Gaucher Disease
NCT01614574
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
- Locations
-
- Hamamatsu University School of Medicine Hamamatsu, Shizuoka, Japan
- The Jikei University School of Medicine Minatoku, Toyko, Japan
- Osaka City University Hospital Osaka, Japan
Completed
Metazym for the Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD)
NCT00418561
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Rigshospitalet Hvidovre, Denmark
NCT03333447
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
- Locations
-
- Beaujon Hospital Clichy, France
NCT00391625
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
- Locations
-
- Shaare Zedek Medical Center Jerusalem, Israel
- Maria Sklodowska Curie Children's Hospital Bucharest, Romania
- Mother and Child Health Care Institute of Serbia Belgrade, Serbia
NCT00937794
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
-
- University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
- Birmingham Children's Hospital Birmingham, United Kingdom