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Clinical trial condition

Lysosomal Storage Diseases

Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.

710 public trials 130 recruiting studies
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Lysosomal Storage Diseases trial results

Completed

Prophylactic Ranibizumab for Exudative Age-related Macular Degeneration

NCT02140151

Conditions
Age-Related Macular Degeneration, Brain Diseases, Brain Diseases, Metabolic, +18 more
Locations
  • Northern California Retina Vitreous Associates Mountain View, California, United States
  • Southern California Desert Retina Consultants Palm Desert, California, United States
  • Elman Retina Baltimore, Maryland, United States
  • Black Hills Regional Eye Institute Rapid City, South Dakota, United States
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Completed

Mucopolysaccharidosis Type II Natural History

NCT03529786

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +22 more
Locations
  • Children's Hospital of Pittsburgh - UPMC: Program for Neurodevelopment in Rare Disorders Pittsburgh, Pennsylvania, United States
  • Hospital de Clinicas de Porto Alegre Porto Alegre, Rio Grande do Sul, Brazil
  • Manchester Centre for Genomic Medicine Manchester, United Kingdom
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Completed

Pharmacokinetics of Alglucosidase Alfa in Patients With Pompe Disease

NCT01410890

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations
  • Investigational Site Number 840008 Valhalla, New York, United States
  • Investigational Site Number 840007 Cincinnati, Ohio, United States
  • Investigational Site Number 840005 Salt Lake City, Utah, United States
  • Investigational Site Number 840003 Fairfax, Virginia, United States
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