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Clinical trial condition

Lysosomal Storage Diseases

Explore clinical trials studying Lysosomal Storage Diseases. Study availability and eligibility vary by location and protocol.

710 public trials 130 recruiting studies
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Lysosomal Storage Diseases trial results

Completed

Genetic Analysis of the Chiari I Malformation

NCT00004738

Conditions
Arnold-Chiari Malformation, Carbohydrate Metabolism, Inborn Errors, Central Nervous System Diseases, +18 more
Locations
  • National Institutes of Health Clinical Center Bethesda, Maryland, United States
  • Kazan State Medical University Kazan', Russia
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Completed

A Study of Intrathecal SHP611 in Children With Metachromatic Leukodystrophy

NCT03771898

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Los Angeles Biomedical Research Institute at Harbor-UCLA Torrance, California, United States
  • Childrens Hospital Colorado Aurora, Colorado, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
  • Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
View all 30 locations
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Completed

Safety and Efficacy of Eliglustat With or Without Imiglucerase in Pediatric Patients With Gaucher Disease (GD) Type 1 and Type 3

NCT03485677

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
Locations
  • Investigational Site Number : 0320001 Buenos Aires, Argentina
  • Investigational Site Number : 1240002 Calgary, Alberta, Canada
  • Investigational Site Number : 1240003 Vancouver, British Columbia, Canada
  • Investigational Site Number : 1240001 Toronto, Ontario, Canada
View all 21 locations
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