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Clinical trial condition

Lipidoses

Explore clinical trials studying Lipidoses. Study availability and eligibility vary by location and protocol.

449 public trials 93 recruiting studies
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Lipidoses trial results

Completed

A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Efficacy of Intracerebroventricular BMN 190 in Patients With Late-Infantile Neuronal Ceroid Lipofuscinosis (CLN2) Disease

NCT01907087

Conditions
Batten Disease, CLN2 Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
Locations
  • Nationwide Children's Hospital Columbus, Ohio, United States
  • University Hamburg-Eppendorf Hamburg, Germany
  • Bambino Gesù Children's Hospital Rome, Italy
  • Guy's & St. Thomas NHS Foundation Trust London, United Kingdom
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Completed

Safety, Tolerability and Pharmacokinetics of SBC-102 (Sebelipase Alfa) in Adult Participants With Lysosomal Acid Lipase Deficiency

NCT01307098

Conditions
Cholesterol Ester Storage Disease, Cholesterol Ester Storage Disease(CESD), Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
Locations
  • Stanford, California, United States
  • New York, United States
  • Pittsburgh, Pennsylvania, United States
  • Prague, Czechia
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