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Clinical trial condition

Lipidoses

Explore clinical trials studying Lipidoses. Study availability and eligibility vary by location and protocol.

11 public trials 2 recruiting studies
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Lipidoses trial results

Completed

Lyso-Gb1 as a Long-term Prognostic Biomarker in Gaucher Disease

NCT02416661

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +16 more
Locations
  • University Hospital Center Mother Teresa Tirana, Albania
  • Aristotle University of Thessaloniki, Ippokration General Hospital Thessaloniki, Greece
  • Centre for Human Genetics Bangalore, India
  • Shaare Zedek Medical Center Jerusalem, Israel
View Trial Details
Completed

Farber Disease Natural History Study

NCT03233841

Conditions
ASAH1 Mutation, Acid Ceramidase Deficiency, Brain Diseases, +27 more
Locations
  • UCSF Benioff Children's Hospital Oakland Oakland, California, United States
  • Children's National Health System Washington D.C., District of Columbia, United States
  • Hospital de Niños de la Santisima Trinidad Córdoba, CP, Argentina
  • Montreal Children's Hospital Montreal, Quebec, Canada
View all 15 locations
View Trial Details
Completed

Safety and Efficacy Study of Sebelipase Alfa in Participants With Lysosomal Acid Lipase Deficiency

NCT02112994

Conditions
Cholesterol Ester Storage Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
Locations
  • Chicago, Illinois, United States
  • Shreveport, Louisiana, United States
  • Cincinnati, Ohio, United States
  • Westmead, Australia
View all 19 locations
View Trial Details
Active, Not Recruiting

Gene Transfer Clinical Trial for Infantile and Late Infantile Krabbe Disease Treated Previously With HSCT

NCT05739643

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations
  • Children's Hospital of Orange County (CHOC) Orange, California, United States
  • University of Michigan Hospitals - Michigan Medicine Ann Arbor, Michigan, United States
  • Duke University Medical Center Durham, North Carolina, United States
View Trial Details

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