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Clinical trial condition

Lipid Metabolism, Inborn Errors

Explore clinical trials studying Lipid Metabolism, Inborn Errors. Study availability and eligibility vary by location and protocol.

834 public trials 155 recruiting studies
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Lipid Metabolism, Inborn Errors trial results

Completed

The Approach Open Label Study: A Study of Volanesorsen (Formerly IONIS-APOCIIIRx) in Participants With Familial Chylomicronemia Syndrome

NCT02658175

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Familial Chylomicronemia Syndrome, +12 more
Locations
  • IONIS Investigative Site Huntington Beach, California, United States
  • IONIS Investigative Site San Francisco, California, United States
  • IONIS Investigative Site Boca Raton, Florida, United States
  • IONIS Investigative Site Boston, Massachusetts, United States
View all 34 locations
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Completed

Treosulfan and Fludarabine Phosphate Before Donor Stem Cell Transplant in Treating Patients With Nonmalignant Inherited Disorders

NCT00919503

Conditions
Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +51 more
Locations
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Oregon Health and Science University Portland, Oregon, United States
  • Vanderbilt University/Ingram Cancer Center Nashville, Tennessee, United States
  • Seattle Children's Hospital Seattle, Washington, United States
View Trial Details
Completed

Replagal Enzyme Replacement Therapy for Children With Fabry Disease

NCT00084084

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
Locations
  • Tucson Access Center of Arizona Kidney Disease Hypertension Center Tucson, Arizona, United States
  • University of Arizona Health Sciences Center Tucson, Arizona, United States
  • Children's Physician Group Palm Beach Gardens, Florida, United States
  • Christus St. Patrick Hospital Lake Charles, Louisiana, United States
View all 14 locations
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Completed

This Study is Designed to Evaluate PD/PK and Safety of Replagal Manufactured by Two Different Processes.

NCT01304277

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • University of Alberta Hospital Edmonton, Alberta, Canada
  • Queen Elizabeth II Health Sciences Centre Halifax, Nova Scotia, Canada
  • The Hospital for Sick Children Toronto, Ontario, Canada
  • INC Research Toronto, Ontario, Canada
View Trial Details

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