NCT04281537
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
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- Amicus Therapeutics, Inc. Philadelphia, Pennsylvania, United States
- Instituto de Genética e Erros Inatos do Metabolismo (IGEIM) São Paulo, Brazil
- Keio University Hospital Tokyo, Japan
- Yokohama Municipal Citizen's Hospital Yokohama, Japan