Enrolling by Invitation
A Study of the Safety and Efficacy of Prime Editing (PM359) in Participants With p47phox Autosomal Recessive Chronic Granulomatous Disease (CGD )
NCT06559176
- Conditions
- Chronic Disease, Chronic Granulomatous Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
- Locations
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- University of California Los Angeles Medical Center Los Angeles, California, United States
- NIH Clinical Center Bethesda, Maryland, United States
- The Children's Hospital at Tristar Medical Group/Sarah Cannon Center for Blood Cancers Nashville, Tennessee, United States
- CHU - Sainte Justine Hospital Montreal, Quebec, Canada