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Clinical trial condition

Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2

Explore clinical trials studying Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2. Study availability and eligibility vary by location and protocol.

4 public trials 0 recruiting studies
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Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2 trial results

Completed

A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Efficacy of Intracerebroventricular BMN 190 in Patients With Late-Infantile Neuronal Ceroid Lipofuscinosis (CLN2) Disease

NCT01907087

Conditions
Batten Disease, CLN2 Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
Locations
  • Nationwide Children's Hospital Columbus, Ohio, United States
  • University Hamburg-Eppendorf Hamburg, Germany
  • Bambino Gesù Children's Hospital Rome, Italy
  • Guy's & St. Thomas NHS Foundation Trust London, United Kingdom
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Active, Not Recruiting

Cerliponase Alfa Observational Study in the US

NCT04476862

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Children's Hospital of Orange County Orange, California, United States
  • Children's Hospital of Colorado Aurora, Colorado, United States
  • Children's National Hospital Washington D.C., District of Columbia, United States
View all 16 locations
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