Completed
Open-Label Extension Study of Trofinetide for the Treatment of Girls and Women With Rett Syndrome
NCT04279314
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
- Locations
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- University of Alabama at Birmingham Birmingham, Alabama, United States
- Translational Genomics Research Institute (TGen) Phoenix, Arizona, United States
- University of California, San Diego La Jolla, California, United States
- UC Davis MIND Institute Sacramento, California, United States