- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +23 more
- Locations
-
- Ann & Robert H Lurie Childrens Hospital of Chicago Chicago, Illinois, United States
- University of North Carolina at Chapel Hill Chapel Hill, North Carolina, United States
- Legacy Emanuel Hospital Portland, Oregon, United States
- Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States
Clinical trial condition
Heredodegenerative Disorders, Nervous System
Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.
1,879 public trials
409 recruiting studies
Heredodegenerative Disorders, Nervous System trial results
NCT05270681
- Conditions
- Basal Ganglia Diseases, Behavior, Brain Diseases, +15 more
- Locations
-
- The Ohio State University Columbus, Ohio, United States
NCT03359213
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
- Locations
-
- Grupo de Pesquisa Clínica em Genética Médica - HCPA Porto Alegre, Brazil
- Igeim - Unifesp São Paulo, Brazil
NCT02777775
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cutaneous Neurofibromas, Genetic Diseases, Inborn, +23 more
- Locations
-
- Spectrum Health Hospital Group Grand Rapids, Michigan, United States
Completed
Adjunctive GNX Treatment Compared With Placebo in Children and Adults With TSC-related Epilepsy
NCT05323734
- Conditions
- Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +13 more
- Locations
-
- Arkansas Children's Research Institute Little Rock, Arkansas, United States
- UCLA Mattel Children's Hospital, TSC Center Los Angeles, California, United States
- Children's Hospital of Orange County Orange, California, United States
- University of California, San Diego San Diego, California, United States
NCT03538041
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Autoimmune, +16 more
- Locations
-
- Georgetown University Hospital Washington D.C., District of Columbia, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Washington University School of Medicine St Louis, Missouri, United States
- Weill Medical College of Cornell University New York, United States
NCT06388291
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +11 more
- Locations
-
- National Hospital of Neurology & Neurosurgery London, United Kingdom
NCT00624234
- Conditions
- Communication Disorders, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslexia, +26 more
- Locations
-
- Vanderbilt University, Vanderbilt University Institute of Imaging Science Nashville, Tennessee, United States
NCT03539952
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +16 more
- Locations
-
- Yale University School of Medicine New Haven, Connecticut, United States
- KU Leuven, Department of Clinical and Experimental Medicine Leuven, Belgium
- Hospital Nossa Senhora das Graças (HNSG) Curitiba, Brazil
- Nucleo de Pesquisa e Desenvolvimento de Medicamentos - Universidade Federal do Ceará - Rodolfo Teófilo Fortaleza, Brazil
NCT07046507
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +16 more
- Locations
-
- Royal Surrey Country Hospital London, United Kingdom