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Heredodegenerative Disorders, Nervous System

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Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,876 public trials 411 recruiting studies

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Heredodegenerative Disorders, Nervous System trial results

Active, Not Recruiting

A Phase I/II Study of VTX-801 in Adult Patients With Wilson's Disease

NCT04537377

Conditions: Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +16 more
Locations: UC Davis Medical Center Sacramento, California, United States

Yale University School of Medecine New Haven, Connecticut, United States

Advent Health Orlando, Florida, United States

University of Michigan Health System Ann Arbor, Michigan, United States

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Active, Not Recruiting

Global Study of Del-desiran for the Treatment of DM1

NCT06411288

Conditions: Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Dystrophy Myotonic, +21 more
Locations: Stanford University Stanford, California, United States

University of Colorado Denver, Colorado, United States

University of Florida Gainesville, Florida, United States

University Research Center of South Florida Tampa, Florida, United States

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Active, Not Recruiting

Feasibility of [11C]Acetate-PET in LAM and TSC

NCT05467397

Conditions: Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +24 more
Locations: Brigham and Women's Hospital Boston, Massachusetts, United States

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SAD of IVT PYC-001 in OPA1 Mutation-Associated Autosomal Dominant Optic Atrophy (Sundew)

NCT06461286

Conditions: Autosomal Dominant Optic Atrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, +16 more
Locations: Save Sight Institute - Sydney Eye Hospital Sydney, New South Wales, Australia

Center for Eye Research Australia (CERA) East Melbourne, Victoria, Australia

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Active, Not Recruiting

A Phase I Clinical Study of ER2001 Injection for the Treatment of Early Manifest Huntington's Disease.

NCT07339514

Conditions: Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +13 more
Locations: First Affiliated Hospital of Guangzhou Medical University Guangzhou, Guangdong, China

First Affiliated Hospital of Sun Yat-sen University Guangzhou, Guangdong, China

West China Hospital of Sichuan University Chengdu, Sichuan, China

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Active, Not Recruiting

Multi-parametric Biomarker Development to Predict Malignant Conversion in Patients With Neurofibromatosis Type 1

NCT05677594

Conditions: Atypical Neurofibroma, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease, +26 more
Locations: Johns Hopkins University Baltimore, Maryland, United States

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MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis

NCT02171104

Conditions: Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more
Locations: Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States

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Study for the Treatment for CLN7 Disease

NCT04737460

Conditions: CLN7, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
Locations: Children' Health Dallas, Texas, United States

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Gene Therapy for Cardiomyopathy Associated With Friedreich's Ataxia

NCT05445323

Conditions: Brain Diseases, Cardiomyopathies, Cardiomyopathy, Secondary, +15 more
Locations: Ataxia Center and HD Center of Excellence, University of California Los Angeles, California, United States

University of South Florida Tampa, Florida, United States

Mayo Clinic Rochester, Minnesota, United States

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Active, Not Recruiting

Amyloidosis TTR Flow Reserve Evaluation

NCT05103943

Conditions: Amyloid Cardiomyopathy, Amyloid Neuropathies, Amyloid Neuropathies, Familial, +13 more
Locations: CHU d'ANGERS Angers, France

CHU Caen Caen, France

CHU Orleans Orléans, France

CHRU de TOURS Tours, France

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Heredodegenerative Disorders, Nervous System

Heredodegenerative Disorders, Nervous System trial results

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