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Clinical trial condition

Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,876 public trials 411 recruiting studies
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Heredodegenerative Disorders, Nervous System trial results

Active, Not Recruiting

Trametinib in Treating Patients With Relapsed or Refractory Juvenile Myelomonocytic Leukemia

NCT03190915

Conditions
Bone Marrow Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +22 more
Locations
  • Children's Hospital of Alabama Birmingham, Alabama, United States
  • Phoenix Childrens Hospital Phoenix, Arizona, United States
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Kaiser Permanente Downey Medical Center Downey, California, United States
View all 57 locations
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Active, Not Recruiting

A Study to Assess the Safety and Tolerability of AZD1390 Given With Radiation Therapy in Patients With Brain Cancer

NCT03423628

Conditions
Astrocytoma, Behavior, Brain Diseases, +31 more
Locations
  • Research Site Boston, Massachusetts, United States
  • Research Site Boston, Massachusetts, United States
  • Research Site New York, United States
  • Research Site Pittsburgh, Pennsylvania, United States
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Active, Not Recruiting

MEK Inhibitor Mirdametinib (PD-0325901) in Patients With Neurofibromatosis Type 1 Associated Plexiform Neurofibromas

NCT03962543

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +18 more
Locations
  • University of Alabama at Birmingham/Children's of Alabama Birmingham, Alabama, United States
  • Mayo Clinic Arizona Phoenix, Arizona, United States
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Children's Hospital Los Angeles Los Angeles, California, United States
View all 43 locations
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Active, Not Recruiting

Long-term Follow-up of Patients With Spinal Muscular Atrophy Treated With OAV101 in Clinical Trials

NCT05335876

Conditions
Atrophy, Bulbo-Spinal Atrophy, X-Linked, Central Nervous System Diseases, +19 more
Locations
  • Child Hosp Of The Kings Daughters Norfolk, Virginia, United States
  • Novartis Investigative Site Sydney, New South Wales, Australia
  • Novartis Investigative Site Leuven, Belgium
  • Novartis Investigative Site Curitiba, Paraná, Brazil
View all 32 locations
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Active, Not Recruiting

A Phase 1/2/3 Study of TSHA-102 Gene Therapy in Females With Rett Syndrome (REVEAL Pivotal Study)

NCT05606614

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +12 more
Locations
  • City of Hope Duarte, California, United States
  • UC San Diego La Jolla, California, United States
  • UC San Francisco Benioff Children's Hospital Oakland, California, United States
  • Rush University Medical Center Chicago, Illinois, United States
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