NCT02890641
- Conditions
- Brain Diseases, Central Nervous System Diseases, Congenital Abnormalities, +26 more
- Locations
-
- Fondation Ophtalmologique Adolphe de Rothschld Paris, France
Clinical trial condition
Heredodegenerative Disorders, Nervous System
Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.
1,876 public trials
411 recruiting studies
Heredodegenerative Disorders, Nervous System trial results
Recruiting
A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
NCT04998396
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +17 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland Oakland, California, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Massachusetts General Hospital (MGH); Center for Rare Neurological Diseases (CRND) Boston, Massachusetts, United States
- Weill Cornell Medicine; Division of Pediatric Neurology New York, United States
NCT07308704
- Conditions
- Amyloid Neuropathies, Amyloid Neuropathies, Familial, Amyloidosis, +20 more
- Locations
-
- Mayo Clinic Rochester, Minnesota, United States
Recruiting
NatiOnal Referral cenTEr Study of Transthyretin Amyloid Cardiomyopathy(ATTR) Patients on Tafamidis
NCT06251778
- Conditions
- ATTR Amyloidosis Wild Type, Amyloid Neuropathies, Amyloid Neuropathies, Familial, +14 more
- Locations
-
- Fondazione IRCCS Policlinico San Matteo Pavia, Italy
NCT06716931
- Conditions
- Behavior, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +12 more
- Locations
-
- Neuromuscular Diagnostic Center. Massachusetts General Hospital Boston, Massachusetts, United States
NCT05849662
- Conditions
- Bone Marrow Diseases, CBL Syndrome, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +24 more
- Locations
-
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Children's Hospital Los Angeles Los Angeles, California, United States
- University of California San Francisco San Francisco, California, United States
- Children's Hospital of Colorado Denver, Colorado, United States
NCT07451613
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +13 more
- Locations
-
- University of California, Irvine Irvine, California, United States
NCT07476365
- Conditions
- Animal Diseases, CMT, CMT (Charcot Marie Tooth Disease), +16 more
- Locations
-
- University Medical Centre Göttingen, Germany
NCT06839469
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), +16 more
- Locations
-
- Stanford University Palo Alto, California, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Columbia University Irving Medical Center New York, United States
NCT07520656
- Conditions
- Abnormalities, Multiple, Aortic Valve Disease, Aortic Valve Stenosis, +30 more
- Locations
-
- Hippocratio General Hospital of Athens Athens, Attica, Greece