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Clinical trial condition

Heredodegenerative Disorders, Nervous System

Explore clinical trials studying Heredodegenerative Disorders, Nervous System. Study availability and eligibility vary by location and protocol.

1,879 public trials 409 recruiting studies
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Heredodegenerative Disorders, Nervous System trial results

Completed

A Study in Subjects With Late Prodromal & Early Manifest HD to Assess the Safety, Tolerability, pk, and Efficacy of Pepi

NCT02481674

Conditions
Basal Ganglia Diseases, Brain Diseases, Central Nervous System Diseases, +17 more
Locations
  • University of Alabama at Birmingham Birmingham, Alabama, United States
  • University of California, San Diego La Jolla, California, United States
  • University of California San Francisco San Francisco, California, United States
  • University of Colorado - Denver Aurora, Colorado, United States
View all 32 locations
View Trial Details
Completed

Clinical Evaluation and Assessment of Instruments and Biomarkers in Subjects With Wilson Disease

NCT04531189

Conditions
Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +16 more
Locations
  • Yale University School of Medicine New Haven, Connecticut, United States
  • Jackson Memorial Hospital Miami Transplant Unit University of Miami Miller School of Medicine Miami, Florida, United States
  • Northwestern University Feinberg School of Medicine Chicago, Illinois, United States
  • University of Michigan Michigan Medicine Hepatology Clinic Taubman Center Ann Arbor, Michigan, United States
View Trial Details
Completed

Mucopolysaccharidosis Type II Natural History

NCT03529786

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +22 more
Locations
  • Children's Hospital of Pittsburgh - UPMC: Program for Neurodevelopment in Rare Disorders Pittsburgh, Pennsylvania, United States
  • Hospital de Clinicas de Porto Alegre Porto Alegre, Rio Grande do Sul, Brazil
  • Manchester Centre for Genomic Medicine Manchester, United Kingdom
View Trial Details
Completed

RAPAMYCIN FOR KIDNEY ANGIOMYOLIPOMAS

NCT00126672

Conditions
Angiomyolipoma, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +20 more
Locations
  • Loma Linda University School of Medicine Loma Linda, California, United States
  • Connecticut Children's Medical Center Hartford, Connecticut, United States
  • Massachusetts General Hospital Boston, Massachusetts, United States
  • New York University Medical Center New York, United States
View Trial Details
Completed

A Study of the Efficacy and Safety of Hematopoietic Stem Cells Transduced With Lenti-D Lentiviral Vector for the Treatment of Cerebral Adrenoleukodystrophy (CALD)

NCT01896102

Conditions
Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
Locations
  • Mattel Children's Hospital UCLA/Ronald Reagan UCLA Medical Center Los Angeles, California, United States
  • Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
  • University of Minnesota Minneapolis, Minnesota, United States
  • Medeos SRL Buenos Aires, Argentina
View Trial Details
Completed

Pomalidomide in Treating Younger Patients With Recurrent, Progressive, or Refractory Central Nervous System Tumors

NCT02415153

Conditions
Central Nervous System Neoplasms, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, +33 more
Locations
  • Children's Hospital Los Angeles Los Angeles, California, United States
  • Lucile Packard Children's Hospital Stanford University Palo Alto, California, United States
  • Children's National Medical Center Washington D.C., District of Columbia, United States
  • Lurie Children's Hospital-Chicago Chicago, Illinois, United States
View Trial Details

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