NCT00683189
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Cooper University Hospital Camden, New Jersey, United States
Clinical trial condition
Hereditary Central Nervous System Demyelinating Diseases
Explore clinical trials studying Hereditary Central Nervous System Demyelinating Diseases. Study availability and eligibility vary by location and protocol.
81 public trials
24 recruiting studies
Hereditary Central Nervous System Demyelinating Diseases trial results
NCT00004378
- Conditions
- Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +47 more
- Locations
-
- University of California Los Angeles Medical Center Los Angeles, California, United States
NCT00006057
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +25 more
- Locations
-
- Mount Sinai School of Medicine New York, United States
Active, Not Recruiting
Treating Leg Symptoms in Women With X-linked Adrenoleukodystrophy
NCT05003648
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +27 more
- Locations
-
- Massachusetts General Hospital Boston, Massachusetts, United States
- University Medical Center of Amsterdam Amsterdam, Netherlands
Active, Not Recruiting
Early Check: Expanded Screening in Newborns
NCT03655223
- Conditions
- 17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
- Locations
-
- RTI International Research Triangle Park, North Carolina, United States
Active, Not Recruiting
Gene Transfer Clinical Trial for Krabbe Disease
NCT04693598
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more
- Locations
-
- University of Michigan Hospitals - Michigan Medicine Ann Arbor, Michigan, United States
Active, Not Recruiting
A Study to Evaluate the Safety and Efficacy of Zilganersen (ION373) in Patients With Alexander Disease (AxD)
NCT04849741
- Conditions
- Alexander Disease, Brain Diseases, Brain Diseases, Metabolic, +13 more
- Locations
-
- Lucile Packard Children's Hospital Stanford Palo Alto, California, United States
- Children's Hospital of Atlanta Atlanta, Georgia, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
Active, Not Recruiting
Diffusion Tensor Imaging (DTI) in Infants With Krabbe Disease
NCT00787865
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +18 more
- Locations
-
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
Active, Not Recruiting
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
NCT02171104
- Conditions
- Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more
- Locations
-
- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
Active, Not Recruiting
OTL-200 in Patients With Late Juvenile Metachromatic Leukodystrophy (MLD)
NCT04283227
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy