NCT03392987
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
- Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy
Clinical trial condition
Hereditary Central Nervous System Demyelinating Diseases
Explore clinical trials studying Hereditary Central Nervous System Demyelinating Diseases. Study availability and eligibility vary by location and protocol.
82 public trials
21 recruiting studies
Hereditary Central Nervous System Demyelinating Diseases trial results
Completed
Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy
NCT01801709
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Bicêtre Hospital - Paris Sud Le Kremlin-Bicêtre, France
NCT01560182
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
- Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy
NCT01325025
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
-
- Unité de recherche biomédicale, Neurospin, I2BM / DSV / SAC/ CEA, Gif-sur-Yvette, France
- Service de Neurologie Pédiatrique, Hôpital Bicêtre Paris, France
- Bâtiment Lavoisier - Unité INSERM U 663,Hôpital Necker Enfants Malades Paris, France
NCT02699190
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
-
- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
Completed
Baby Detect : Genomic Newborn Screening
NCT05687474
- Conditions
- 3-Hydroxy 3-Methyl Glutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, 3-Hydroxy-3-Methylglutaryl-CoA Synthase 2 Deficiency, +368 more
- Locations
-
- CRMN, Hôpital La Citadelle Liège, Wallonia, Belgium
NCT04628364
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +23 more
- Locations
-
- National Organization for Rare Disorders Danbury, Connecticut, United States
Completed
A Clinical Study to Evaluate the Efficacy and Safety of MIN-102 (IMP) in Male AMN Patients.
NCT03231878
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +21 more
- Locations
-
- Stanford University Medical Center Stanford, California, United States
- Kennedy Krieger Institute Baltimore, Maryland, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
- Hospital de la Pitié-Salpêtrière Paris, France
NCT03852498
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
-
- Lucile Packard Children's Hospital Palo Alto, California, United States
- Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Hôpital Robert Debré Paris, France
NCT04687007
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
-
- Leipzig University Medical Center, Leukodystrophy Outpatient Clinic, Department of Neurology, Leipzig, Germany Leipzig, Saxony, Germany
- Leukodystrophy Outpatient Clinic Leipzig, Germany