Active, Not Recruiting
Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1 Gangliosidosis
NCT04713475
- Conditions
- Beta-Galactosidase-1 (GLB1) Deficiency, Brain Diseases, Brain Diseases, Metabolic, +23 more
- Locations
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- Benioff Children's Hospital Oakland, California, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Children's Hospital at St. Peter's University Hospital New Brunswick, New Jersey, United States
- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States