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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,537 public trials 2,139 recruiting studies
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Genetic Diseases, Inborn trial results

Recruiting

A Study to Learn About the Safety and Effects of the Study Drug PRX-102 in Children and Adolescents With Fabry Disease

NCT06328608

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Phoenix Children's Phoenix, Arizona, United States
  • Emory Genetics Clinical Trials Center Atlanta, Georgia, United States
  • University of Iowa Iowa City, Iowa, United States
  • Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
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Recruiting

Maternal and Postnatal Outcomes Study (MOS): A Global Observational Registry Assessing the Safety of Elfabrio® in Women With Fabry Disease and Their Infants During Pregnancy and Breastfeeding

NCT06941025

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +23 more
Locations
  • No physical study sites - Decentralized, web-based registry Washington D.C., District of Columbia, United States
  • No physical study sites - Decentralized, web-based registry Berlin, Germany
  • No physical study sites - Decentralized, web-based registry Rome, Italy
  • No physical study sites - Decentralized, web-based registry Madrid, Spain
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Recruiting

Spastic Paraplegia - Centers of Excellence Research Network

NCT06553976

Conditions
Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Early Onset Hereditary Spastic Paraplegia, +18 more
Locations
  • University of Miami Miller School of Medicine Miami, Florida, United States
  • University of Iowa Carver College of Medicine Iowa City, Iowa, United States
  • Boston Children's Hospital Boston, Massachusetts, United States
  • Massachusetts General Hospital Boston, Massachusetts, United States
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Recruiting

Performance of the Cardiac Microcurrent (C-MIC) System With a Less Invasively Placed Left Ventricular Lead

NCT06920030

Conditions
Cardiomegaly, Cardiomyopathies, Cardiomyopathy, Dilated, +9 more
Locations
  • University Clinical Center of the Republic of Srbska Banja Luka, Republic of Srbska, Bosnia and Herzegovina
  • Institute of Cardiovascular Disease Dedinje Belgrade, Serbia
  • Clinical Hospital Center Bezanijska kosa Belgrade, Serbia
  • UKC Kragujevac Kragujevac, Serbia
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Recruiting

Study to Evaluate the Safety, PK, PD, and Efficacy of PRX-102 in Japanese Patients With Fabry Disease

NCT05710692

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Fukuoka University Chikushi Hospital Chikushino-shi, Fukuoka, Japan
  • Tohoku University Hospital Sendai, Miyagi, Japan
  • University of the Ryukyu Hospital Nishihara, Okinawa, Japan
  • Osaka University Hospital Suita, Osaka, Japan
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