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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,537 public trials 2,139 recruiting studies
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Genetic Diseases, Inborn trial results

Recruiting

Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety of a Single Intravitreal Injection of RTx-021 in Patients With Stargardt Disease

NCT07439887

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Eye Diseases, Hereditary, +5 more
Locations
  • RayTx Clinical Site Bakersfield, California, United States
  • UPMC Vision Institute Pittsburgh, Pennsylvania, United States
  • RayTx Clinical Site Bellaire, Texas, United States
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Recruiting

Treatment of Refractory BK Infections With Related Donor BK Specific Cytotoxic T-cells (CTLs)

NCT04197596

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Immune System Diseases, +6 more
Locations
  • University of California San Francisco San Francisco, California, United States
  • Johns Hopkins Baltimore, Maryland, United States
  • Washington University St Louis, Missouri, United States
  • New York Medical College Vallhala, New York, United States
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Recruiting

A Phase I/II Study of Trametinib and Azacitidine for Patients With Newly Diagnosed Juvenile Myelomonocytic Leukemia

NCT05849662

Conditions
Bone Marrow Diseases, CBL Syndrome, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +24 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Children's Hospital Los Angeles Los Angeles, California, United States
  • University of California San Francisco San Francisco, California, United States
  • Children's Hospital of Colorado Denver, Colorado, United States
View all 19 locations
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