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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,674 public trials 2,143 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

A Study to Assess the Efficacy and Safety of Vamorolone in Boys With Duchenne Muscular Dystrophy (DMD)

NCT03439670

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • University of California Davis Davis, California, United States
  • University of California Los Angeles Los Angeles, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Nemours Children's Hospital Orlando, Florida, United States
View all 33 locations
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Completed

Tele-Coaching Intervention to Improve Treatment Adherence in Cystic Fibrosis

NCT03921229

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cystic Fibrosis, Digestive System Diseases, +5 more
Locations
  • Stanford University Palo Alto, California, United States
  • National Jewish Health Denver, Colorado, United States
  • Northwestern University Chicago, Illinois, United States
  • University of Kansas Medical Center Kansas City, Kansas, United States
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Completed

A Study to Evaluate Long-Term Maintenance Treatment With Once Daily Crisaborole Ointment 2% in Pediatric and Adult Participants With Mild-to-Moderate Atopic Dermatitis

NCT04040192

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +10 more
Locations
  • First OC Dermatology Fountain Valley, California, United States
  • Center for Dermatology Clinical Research, Inc. Fremont, California, United States
  • Asthma and Allergy Associates, PC Colorado Springs, Colorado, United States
  • Colorado Springs Dermatology Clinic, PC Colorado Springs, Colorado, United States
View all 44 locations
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Completed

Study of Octaplex, a Four-factor Prothrombin Complex Concentrate (4F-PCC) and Beriplex® P/N (Kcentra) for the Reversal of Vitamin K Antagonist (VKA) Induced Anticoagulation in Patients Needing Urgent Surgery With Significant Bleeding Risk.

NCT02740335

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +8 more
Locations
  • Octapharma Research Site Aurora, Colorado, United States
  • Octapharma Research Site New Haven, Connecticut, United States
  • Octapharma Research Site Miami, Florida, United States
  • Octapharma Research Site Tampa, Florida, United States
View all 86 locations
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Completed

Phenylalanine and Its Impact on Cognition

NCT03788343

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
Locations
  • Department of Diabetes, Endocrinology, Nutritional Medicine and Metabolism (UDEM), Inselspital, Bern University Hospital Bern, Switzerland
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