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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,674 public trials 2,143 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

Patient Characteristics and Treatment Patterns From Early Crizanlizumab Use in Real-world Setting: Preliminary Analysis From Select Sickle Cell Centers

NCT05833022

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +7 more
Locations
  • University of Alabama Birmingham Birmingham, Alabama, United States
  • Cristiana Care Wilmington, Delaware, United States
  • All Children's Hospital St. Petersburg, Florida, United States
  • Johns Hopkins University Baltimore, Maryland, United States
View Trial Details
Completed

Selumetinib Paediatric NF1 Japan Study

NCT04495127

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +14 more
Locations
  • Research Site Minatoku, Japan
  • Research Site Nagoya, Japan
  • Research Site Setagaya-ku, Japan
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Completed

Study to Assess the Efficacy and Safety of Raxone in LHON Patients

NCT02774005

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, Eye Diseases, +13 more
Locations
  • Retinal Consultants of Arizona Phoenix, Arizona, United States
  • Palo Alto Medical Foundation Palo Alto, California, United States
  • Stanford Byers Eye Institute Stanford, California, United States
  • University of Colorado Health Eye Center Aurora, Colorado, United States
View all 29 locations
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Completed

A Pharmacokinetics and Safety Study of Nemolizumab in Adolescent Participants With Atopic Dermatitis (AD)

NCT03921411

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • Galderma Investigational Site Fountain Valley, California, United States
  • Galderma Investigational Site Fremont, California, United States
  • Galderma Investigational Site Jacksonville, Florida, United States
  • Galderma Investigational Site Tampa, Florida, United States
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