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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,633 public trials 2,161 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

A Study to Investigate the Efficacy and Safety of ZX008 (Fenfluramine Hydrochloride) as an Adjunctive Therapy in Children and Adults With Lennox-Gastaut Syndrome

NCT03355209

Conditions
Brain Diseases, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +5 more
Locations
  • Ep0214 107 Tucson, Arizona, United States
  • Ep0214 144 Los Angeles, California, United States
  • Ep0214 101 San Francisco, California, United States
  • Ep0214 103 Aurora, Colorado, United States
View all 72 locations
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Completed

Towards Optimal Treatment of Marfan Syndrome

NCT05944614

Conditions
Abnormalities, Multiple, Aortic Diseases, Bone Diseases, +13 more
Locations
  • Radboud University Medical Center Nijmegen, Gelderland, Netherlands
  • Leiden University Medical Center Leiden, North Holland, Netherlands
  • Amsterdam UMC, location AMC Amsterdam, Netherlands
  • University Medical Center Groningen Groningen, Netherlands
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Completed

Trientine Tetrahydrochloride (TETA 4HCL) for the Treatment of Wilson's Disease

NCT03539952

Conditions
Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +16 more
Locations
  • Yale University School of Medicine New Haven, Connecticut, United States
  • KU Leuven, Department of Clinical and Experimental Medicine Leuven, Belgium
  • Hospital Nossa Senhora das Graças (HNSG) Curitiba, Brazil
  • Nucleo de Pesquisa e Desenvolvimento de Medicamentos - Universidade Federal do Ceará - Rodolfo Teófilo Fortaleza, Brazil
View all 15 locations
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Completed

Eucrisa for Atopic Dermatitis

NCT03250663

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, Dermatitis, Atopic, +9 more
Locations
  • Wake Forest University Heath Sciences Winston-Salem, North Carolina, United States
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Completed

Efficacy and Safety of Lonigutamab in Subjects With Thyroid Eye Disease (TED)

NCT05683496

Conditions
Autoimmune Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Endocrine System Diseases, +12 more
Locations
  • Clinical Research Site Jacksonville, Florida, United States
  • Clinical Research Site Atlanta, Georgia, United States
  • Clinical Research Site Ann Arbor, Michigan, United States
  • Clinical Research Site East Setauket, New York, United States
View Trial Details

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