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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,633 public trials 2,161 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

A Non-Interventional National Study in Pediatric Patients With Unexplained Enlarged Spleen

NCT04845958

Conditions
Acid Sphingomyelinase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +25 more
Locations
  • Investigational Site Number 2500036 Amiens, France
  • Investigational Site Number 2500014 Angers, France
  • Investigational Site Number 2500034 Argenteuil, France
  • Investigational Site Number 2500039 Bayonne, France
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Completed

A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US

NCT03597399

Conditions
Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, +7 more
Locations
  • Children's Hospital of Los Angeles Los Angeles, California, United States
  • Bascom Palmer Eye Institute Miami, Florida, United States
  • University of Iowa Hospitals & Clinics Iowa City, Iowa, United States
  • Massachusetts Eye and Ear Institute Boston, Massachusetts, United States
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Completed

Randomized Study to Evaluate the Effect of Obicetrapib on Top of Maximum Tolerated Lipid-Modifying Therapies

NCT05142722

Conditions
Arterial Occlusive Diseases, Arteriosclerosis, Atherosclerosis, +17 more
Locations
  • Pinnacle Research Group Anniston, Alabama, United States
  • Central Alabama Research Birmingham, Alabama, United States
  • Synexus Clinical Research US, Inc. / Simon Williamson Clinic, PC Birmingham, Alabama, United States
  • The Center for Clinical Trials, Inc Saraland, Alabama, United States
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