Skip to main content
OpenTrials

Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,629 public trials 2,161 recruiting studies
Refine in advanced search Browse all conditions

Genetic Diseases, Inborn trial results

Completed

A Study of TAK-625 for the Treatment of Alagille Syndrome (ALGS)

NCT05543174

Conditions
Abnormalities, Multiple, Alagille Syndrome, Alagille Syndrome (ALGS), +12 more
Locations
  • University of Tsukuba Hospital Tsukuba, Ibaraki, Japan
  • Yokohamashi Tobu Hospital Yokohama, Kanagawa, Japan
  • Miyagi Children's Hospital Sendai, Miyagi, Japan
  • Kindai University Nara Hospital Ikoma, Nara, Japan
View Trial Details
Completed

Safety, PK, PD, and Clinical Activity of Orally Administered KT-621 in Adult Patients With Atopic Dermatitis (AD)

NCT06945458

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • Kymera Investigative Site Birmingham, Alabama, United States
  • Kymera Investigative Site Fountain Valley, California, United States
  • Kymera Investigative Site Santa Monica, California, United States
  • Kymera Investigative Site Boynton Beach, Florida, United States
View Trial Details
Completed

Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies

NCT03837184

Conditions
Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
Locations
  • Tokyo Women's Medical University Tokyo, Japan
  • Pusan National University Yangsan Hospital Yangsan, Gyeongsangnam-do, South Korea
  • Seoul National University Hospital Seoul, South Korea
  • National Taiwan University Hospital Taipei, Taiwan
View Trial Details

Related conditions