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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,530 public trials 2,140 recruiting studies
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Genetic Diseases, Inborn trial results

Recruiting

A Study to Investigate the Safety, Pharmacokinetics, and Preliminary Efficacy of IDE574 Therapy in Adult Participants With Advanced Solid Tumors

NCT07540572

Conditions
Brain Diseases, Bronchial Neoplasms, Carcinoma, Bronchogenic, +30 more
Locations
  • Florida Clinical Trials Group Plantation, Florida, United States
  • START Astera, LLC East Brunswick, New Jersey, United States
  • START New York Long Island, LLC Lake Success, New York, United States
  • NEXT Texas LLC - Austin Austin, Texas, United States
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Recruiting

Evaluate Efficacy and Safety of Repeat Subcutaneous Doses of FB825 in Adults With Moderate-to-Severe Atopic Dermatitis

NCT06397911

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • First OC Dermatology Fountain Valley, California, United States
  • Center for Dermatology Clinical Research, Inc. Fremont, California, United States
  • California Allergy and Asthma Medical Group Los Angeles, California, United States
  • University of California, Davis Health, Department of Dermatology Sacramento, California, United States
View all 16 locations
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Recruiting

Ganciclovir Resistant/Refractory Cytomegalovirus Infection in SOT Recipients and HSCT Patients

NCT05234723

Conditions
Amino Acid Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cytomegalovirus Infections, +10 more
Locations
  • MD Anderson Cancer Center Houston, Texas, United States
  • Institut Jules Bordet Brussels, Belgium
  • University Hospitals Leuven Leuven, Belgium
  • Helsinki University Central Hospital Helsinki, Finland
View all 23 locations
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Recruiting

Autosomal Dominant Polycystic Kidney Disease (ADPKD) Study

NCT04338048

Conditions
ADPKD, Abnormalities, Multiple, Ciliopathies, +12 more
Locations
  • Children's National Hospital Washington D.C., District of Columbia, United States
  • Mayo Clinic Rochester, Minnesota, United States
  • Cohen Children's Medical Center New Hyde Park, New York, United States
  • Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
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Recruiting

An Open-label, Multicenter Phase I/II Clinical Trial to Evaluate the Safety, Tolerability, Efficacy, and Pharmacokinetic/Pharmacodynamic (PK/PD) Characteristics of SR604 Injection in Patients With Hemophilia A/B and Congenital Factor VII Deficiency

NCT07644832

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +9 more
Locations
  • Xiangya Hospital of Central South University Changsha, China
  • The First Affiliated Hospital of University of Science and Technology of China Hefei, China
  • Jinan Central Hospital Jinan, China
  • The First Hospital of Lanzhou University Lanzhou, China
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Recruiting

Testing for Safety and Colorectal Cancer Preventive Effects of ONC201

NCT05630794

Conditions
Adenoma, Adenomatous Polyposis Coli, Adenomatous Polyps, +21 more
Locations
  • University of Michigan Rogel Cancer Center Ann Arbor, Michigan, United States
  • Washington University School of Medicine St Louis, Missouri, United States
  • Cleveland Clinic Foundation Cleveland, Ohio, United States
  • Ohio State University Comprehensive Cancer Center Columbus, Ohio, United States
View Trial Details

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