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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,627 public trials 2,162 recruiting studies
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Genetic Diseases, Inborn trial results

Completed

Efficacy & Safety Study of Bilateral IVT Injection of GS010 in LHON Subjects Due to the ND4 Mutation for up to 1 Year

NCT03293524

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, Eye Diseases, +13 more
Locations
  • Doheny Eye Center UCLA Pasadena Pasadena, California, United States
  • University of Colorado Health Eye Center Aurora, Colorado, United States
  • Emory Healthcare - The Emory Clinic Atlanta, Georgia, United States
  • Massachusetts Eye and Ear Infirmary Boston, Massachusetts, United States
View all 13 locations
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Completed

Nedosiran in Pediatric Patients From Birth to 11 Years of Age With PH and Relatively Intact Renal Function

NCT05001269

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, +17 more
Locations
  • Clinical Research Site Rochester, Minnesota, United States
  • Clinical Research Site Hamilton, Ontario, Canada
  • Clinical Trial Site Bonn, Germany
  • Clinical Research Site Heidelberg, Germany
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Completed

Zimura Compared to Sham in Patients With Autosomal Recessive Stargardt Disease (STGD1)

NCT03364153

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Eye Diseases, Hereditary, +6 more
Locations
  • Retinal Research Institute Phoenix, Arizona, United States
  • Jules Stein Eye Institute/ David Geffen School of Medicine Los Angeles, California, United States
  • VitreoRetinal Associates Gainesville, Florida, United States
  • Retina Specialty Institute Pensacola, Florida, United States
View all 41 locations
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