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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,520 public trials 2,145 recruiting studies
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Genetic Diseases, Inborn trial results

Recruiting

Natural History of Sickle Cell Disease

NCT00081523

Conditions
Acute Chest Syndrome, Anemia, Anemia, Hemolytic, +15 more
Locations
  • Childrens National Health Center Washington D.C., District of Columbia, United States
  • Suburban Hospital Bethesda, Maryland, United States
  • National Institutes of Health Clinical Center Bethesda, Maryland, United States
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Recruiting

Danon Disease Natural History Study

NCT06214507

Conditions
Carbohydrate Metabolism, Inborn Errors, Cardiomyopathies, Cardiovascular Diseases, +15 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • University of California, San Diego La Jolla, California, United States
  • Children's Hospital Colorado Aurora, Colorado, United States
  • University of Florida College of Medicine Gainesville, Florida, United States
View all 15 locations
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Recruiting

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

NCT07486934

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +18 more
Locations
  • UCSD - Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Rare Disease Research, LLC Atlanta, Georgia, United States
  • IU Health Neuroscience Center Indianapolis, Indiana, United States
  • Roy Blunt NextGen Precision Health Institute Columbia, Missouri, United States
View all 21 locations
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