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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,613 public trials 2,162 recruiting studies
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Genetic Diseases, Inborn trial results

Active, not recruiting

AV-23-001 AVAVA MIRIA Pilot Study

NCT06557434

Conditions
Acne Scars - Mixed Atrophic and Hypertrophic, Cicatrix, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +15 more
Locations
  • Skinfluence Long Island Dix Hills, New York, United States
  • Laser and Skin Surgery Center of New York New York, United States
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Active, not recruiting

FCN-159 in Adult Patients With Symptomatic, Inoperable Neurofibromatosis Type 1-Related Plexiform Neurofibromas

NCT05913037

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +18 more
Locations
  • Cancer Hospital Chinese Academy of Medical Sciences Beijing, Beijing Municipality, China
  • Chinese Academy of Medical Sciences & Peking Union Medical College Beijing, Beijing Municipality, China
  • Plastic Surgery Hospital,Chinese Academy of Medical Sciences Beijing, Beijing Municipality, China
  • Nanfang Hospital, Southern Medical University Guangzhou, Guangdong, China
View all 15 locations
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Active, not recruiting

Gene Therapy for Haemophilia A.

NCT03001830

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +6 more
Locations
  • St. Luke'S Regional Medical Center, Ltd Boise, Idaho, United States
  • University of Kentucky Lexington, Kentucky, United States
  • St Jude's Children's Research Hospital Memphis, Tennessee, United States
  • Royal Free Hospital London, United Kingdom
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Active, not recruiting

An Observational Study to Assess Change in Disease Activity and Use of Upadacitinib Tablets in Adolescent and Adult Participants With Moderate to Severe Atopic Dermatitis in Real World

NCT05669794

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • Ch Saint Quentin /Id# 249270 Saint-Quentin, Aisne, France
  • CHU Clermont-Ferrand /ID# 248611 Clermont, Auvergne-Rhône-Alpes, France
  • Hôpital Européen Marseille /ID# 257643 Marseille, Bouches-du-Rhone, France
  • Hopital Saint Joseph /ID# 255537 Marseille, Bouches-du-Rhone, France
View all 59 locations
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Active, not recruiting

Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product

NCT02698579

Conditions
Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +24 more
Locations
  • Mattel Children's Hospital-UCLA Los Angeles, California, United States
  • Lucile Packard Children's Hospital - Stanford Palo Alto, California, United States
  • Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
  • University of Minnesota Minneapolis, Minnesota, United States
View all 13 locations
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