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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,603 public trials 2,158 recruiting studies
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Genetic Diseases, Inborn trial results

Active, not recruiting

Open-Label Study of AG10 in Patients with Cardiomyopathy

NCT03536767

Conditions
Amyloid Cardiomyopathy, Amyloid Neuropathies, Amyloid Neuropathies, Familial, +13 more
Locations
  • Stanford University Palo Alto, California, United States
  • University of California San Francisco San Francisco, California, United States
  • Yale University New Haven, Connecticut, United States
  • Northwestern University Chicago, Illinois, United States
View Trial Details
Active, not recruiting

Cardiac Structure and Function in Patients with Cystic Fibrosis

NCT06084468

Conditions
Brain Diseases, Cardiovascular Diseases, Central Nervous System Diseases, +31 more
Locations
  • Department of Cardiology, Herlev and Gentofte University Hospital, University of Copenhagen Hellerup, Copenhagen, Denmark
  • Department of Infectious Diseases, University Hospital of Copenhagen, Cystic Fibrosis Centre, Copenhagen, Denmark Copenhagen, Denmark
View Trial Details
Active, not recruiting

AV-23-001 AVAVA MIRIA Pilot Study

NCT06557434

Conditions
Acne Scars - Mixed Atrophic and Hypertrophic, Cicatrix, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +15 more
Locations
  • Skinfluence Long Island Dix Hills, New York, United States
  • Laser and Skin Surgery Center of New York New York, United States
View Trial Details
Active, not recruiting

FCN-159 in Adult Patients With Symptomatic, Inoperable Neurofibromatosis Type 1-Related Plexiform Neurofibromas

NCT05913037

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +18 more
Locations
  • Cancer Hospital Chinese Academy of Medical Sciences Beijing, Beijing Municipality, China
  • Chinese Academy of Medical Sciences & Peking Union Medical College Beijing, Beijing Municipality, China
  • Plastic Surgery Hospital,Chinese Academy of Medical Sciences Beijing, Beijing Municipality, China
  • Nanfang Hospital, Southern Medical University Guangzhou, Guangdong, China
View all 15 locations
View Trial Details
Active, not recruiting

Gene Therapy for Haemophilia A.

NCT03001830

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Coagulation Protein Disorders, +6 more
Locations
  • St. Luke'S Regional Medical Center, Ltd Boise, Idaho, United States
  • University of Kentucky Lexington, Kentucky, United States
  • St Jude's Children's Research Hospital Memphis, Tennessee, United States
  • Royal Free Hospital London, United Kingdom
View Trial Details

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