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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,522 public trials 2,142 recruiting studies
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Genetic Diseases, Inborn trial results

Recruiting

Phase 1b Study of VERVE-201 in Patients With Refractory Hyperlipidemia

NCT06451770

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Genetic Diseases, Inborn, +11 more
Locations
  • Clinical Study Center Clearwater, Florida, United States
  • Clinical Study Center Miami Lakes, Florida, United States
  • Clinical Study Center Port Orange, Florida, United States
  • Clinical Study Center New York, United States
View all 16 locations
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Recruiting

FORTIFI-HN01: A Study of Ficerafusp Alfa (BCA101) or Placebo in Combination With Pembrolizumab in First-Line PD-L1-pos, R or M HNSCC

NCT06788990

Conditions
Bone Diseases, Bone Diseases, Developmental, Camurati-Engelmann Syndrome, +17 more
Locations
  • Site # 0137 Birmingham, Alabama, United States
  • Site #0147 Phoenix, Arizona, United States
  • Site #0107 La Jolla, California, United States
  • Site #0106 Los Angeles, California, United States
View all 203 locations
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Recruiting

Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH

NCT02716246

Conditions
Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
Locations
  • Nationwide Children's Hospital Columbus, Ohio, United States
  • Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
  • Women's and Children's Hospital North Adelaide, South Australia, Australia
  • Vall d'Hebron Barcelona Hospital Campus Barcelona, Spain
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Recruiting

Genetic Basis of Immunodeficiency

NCT00055172

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Repair-Deficiency Disorders, Genetic Diseases, Inborn, +7 more
Locations
  • National Institutes of Health Clinical Center Bethesda, Maryland, United States
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Recruiting

A Study to Learn How Stargardt-type Eye Conditions Progress in Children and Adults

NCT07425574

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Eye Diseases, Eye Diseases, Hereditary, +7 more
Locations
  • Associated Retina Consultants Phoenix, Arizona, United States
  • Stanford University School of Medicine Palo Alto, California, United States
  • University of California Health - UC Davis Sacramento, California, United States
  • University of Illinois Chicago - UI Health Chicago, Illinois, United States
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Recruiting

A Dose-ranging Study to Evaluate the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Galvokimig in Adult Study Participants With Atopic Dermatitis

NCT07277660

Conditions
Atopic Dermatitis, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, +9 more
Locations
  • Atd002 52021 Oceanside, California, United States
  • Atd002 52008 Santa Monica, California, United States
  • Atd002 52013 Boca Raton, Florida, United States
  • Atd002 52007 Miami, Florida, United States
View all 68 locations
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Recruiting

PregnAncy-Related Aortic DISsEction in China

NCT07672210

Conditions
Abnormalities, Multiple, Acute Aortic Syndrome, Aneurysm, +37 more
Locations
  • DeltaHealth Hospital Shanghai Shanghai, Shanghai Municipality, China
  • Beijing Anzhen Hospital Beijing, China
  • Guangdong Provincial Hospital Guangzhou, China
  • Wuhan Union Hospital Wuhan, China
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