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Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,522 public trials 2,142 recruiting studies
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Genetic Diseases, Inborn trial results

Recruiting

A Phase I/II Study of ITU512 in Healthy Participants and Patients With Sickle Cell Disease

NCT06546670

Conditions
Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +7 more
Locations
  • University of Alabama Birmingham Birmingham, Alabama, United States
  • Quotient Sciences Sea View Miami, Florida, United States
  • Boston Childrens Hospital Boston, Massachusetts, United States
  • East Carolina University Greenville, North Carolina, United States
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Recruiting

Clinical and Demographic Characteristics of Adult p Atients With NEurofibromatosis in RUSsia

NCT07088991

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +11 more
Locations
  • Research Site Arkhangelsk, Russia
  • Research Site Chelyabinsk, Russia
  • Research Site Grozny, Russia
  • Research Site Krasnoyarsk, Russia
View all 16 locations
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Recruiting

Study of Skeletal Disorders

NCT05031507

Conditions
Bone Diseases, Bone Diseases, Developmental, Carbohydrate Metabolism, Inborn Errors, +15 more
Locations
  • National Institutes of Health Clinical Center Bethesda, Maryland, United States
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Recruiting

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

NCT06564974

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Arkansas Childrens Hospital Little Rock, Arkansas, United States
  • Loma Linda University Pediatric Subspecialty Clinics Loma Linda, California, United States
  • Children's Hospital Los Angeles Los Angeles, California, United States
View all 33 locations
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