Skip to main content
OpenTrials

Clinical trial condition

Genetic Diseases, Inborn

Explore clinical trials studying Genetic Diseases, Inborn. Study availability and eligibility vary by location and protocol.

12,553 public trials 2,147 recruiting studies
Refine in advanced search Browse all conditions

Genetic Diseases, Inborn trial results

Recruiting

CfDNA in Hereditary And High-risk Malignancies 2

NCT06726642

Conditions
Adnexal Diseases, Breast Diseases, Breast Neoplasms, +36 more
Locations
  • BC Cancer Agency Vancouver, British Columbia, Canada
  • Eastern Health St. John's, Newfoundland and Labrador, Canada
  • IWK Health Centre Halifax, Nova Scotia, Canada
  • The Hospital for Sick Children Toronto, Ontario, Canada
View Trial Details
Recruiting

Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)

NCT04906460

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
Locations
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • Rare Disease Research LLC Atlanta, Georgia, United States
  • Istiklal Hospital/ Clinical Research Unit Amman, Jordan
  • The Specialty Hospital (TSH)/ Advanced Clinical Center Amman, Jordan
View Trial Details
Recruiting

Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)

NCT06150716

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +12 more
Locations
  • Ionis Investigative Site Atlanta, Georgia, United States
  • Ionis Investigative Site Philadelphia, Pennsylvania, United States
  • Ionis Investigative Site Salt Lake City, Utah, United States
  • Ionis Investigative Site Le Kremlin-Bicêtre, France
View Trial Details

Related conditions