NCT00001405
- Conditions
- Chronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, +18 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Clinical trial condition
Genetic Disease, Inborn
Explore clinical trials studying Genetic Disease, Inborn. Study availability and eligibility vary by location and protocol.
5 public trials
3 recruiting studies
Genetic Disease, Inborn trial results
NCT07608432
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DMD, Duchenne Muscular Dystrophy (DMD), +21 more
- Locations
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- Rare Disease Research, LLC Hillsborough, North Carolina, United States
Recruiting
A Phase 3 Study of NTLA-2001 in ATTRv-PN
NCT06672237
- Conditions
- Amyloid Neuropathies, Amyloid Neuropathies, Familial, Amyloidosis, +23 more
- Locations
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- Hospital Británico de Buenos Aires Buenos Aires, Argentina
- Hospital Italiano de Buenos Aires (HIBA) Buenos Aires, Argentina
- Hospital El Cruce San Juan Bautista, Argentina
- Hospital das Clinicas da Universidade Estadual de Campinas (UNICAMP) Campinas, Brazil
NCT05425745
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyslipidemias, Familial Hypercholesterolemia, +14 more
- Locations
-
- Site 01022 Jonesboro, Arkansas, United States
- Site 01015 Toluca Lake, California, United States
- Site 01009 Sarasota, Florida, United States
- Site 01023 Boise, Idaho, United States
NCT02916888
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dermatitis, Dermatitis, Atopic, +10 more
- Locations
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- Yale Dermatology Associates New Haven, Connecticut, United States